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Gene Details

TPMT

TPMT metabolizes thiopurine drugs used in leukemia treatment and autoimmune diseases. Variants in TPMT can lead to severe bone marrow toxicity if dosing isn't adjusted.

Affected Medications (2)
Variants & Recommendations

*3A, *3B (heterozygous loss of function)

Intermediate Metabolizer

ADJUST DOSE

Drug

Azathioprine

Effect

Myelosuppression risk (intermediate)

Recommendation

ADJUST. Standard dose with close monitoring.

CPIC Guideline

CPIC Level B

FDA Label

Monitor CBC closely

*3A, *3B, *3C (loss of function)

Poor Metabolizer

AVOID

Drug

Azathioprine

Effect

Increased thioguanine nucleotides → severe myelosuppression

Recommendation

AVOID or reduce dose by 90%.

CPIC Guideline

CPIC Level A

FDA Label

Black box warning: test before use

*3A, *3B, *3C (loss of function)

Poor Metabolizer

AVOID

Drug

Mercaptopurine

Effect

Severe myelosuppression risk

Recommendation

AVOID or reduce dose by 90%.

CPIC Guideline

CPIC Level A

FDA Label

Black box warning: test before use

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